VERBRINACOGENE SETPARVOVEC

UNII:	KT8AC75KUX
Formula:
Preferred Substance Name:	VERBRINACOGENE SETPARVOVEC
GSRS Full Record:	KT8AC75KUX i

2364604-87-3
A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS OF A MODIFIED LIVER-TROPIC SEROTYPE (S3) (RAAV REP2-CAPS3) VECTOR, ENCODING A GAIN-OF-FUNCTION VARIANT (R338LPADUA) OF CODON-OPTIMISED HUMAN COAGULATION FACTOR IX (HFIX) UNDER THE CONTROL OF A LIVER-SPECIFIC PROMOTER (FRE1) COMPRISING A TRUNCATED VERSION OF THE HUMAN APOLIPOPROTEIN E LOCUS CONTROL REGION (I.E. ENHANCER) WITH A TRUNCATED VERSION OF THE HUMAN ALPHA-1-ANTITRYPSIN PROMOTE
DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS AAVS3-FLT180A VECTOR HUMAN BLOOD-COAGULATION FACTOR IX PADUA-SPECIFYING)
FLT180A
FLT-180A
VERBRINACOGENE SETPARVOVEC [INN]
VERBRINACOGENE SETPARVOVEC [USAN]

Note

UNIIs are generated based on scientific identity characteristics using ISO 11238 data elements. UNII availability does not imply any regulatory review or approval. Synonyms and mappings are based on the best public information available at the time of publication. Please report any problems/errors associated with this data to FDA-SRS@fda.hhs.gov.

VERBRINACOGENE SETPARVOVEC

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