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PASEMNOGENE GLEPARVOVEC TRANSGENE INSERT ENCODING CODON-OPTIMISED HUMAN SURVIVAL OF MOTOR NEURON 1 (SMN1) GENE

UNII:JZW2TY9A6W
Type:INGREDIENT SUBSTANCE
Formula:
Preferred Substance Name:PASEMNOGENE GLEPARVOVEC TRANSGENE INSERT ENCODING CODON-OPTIMISED HUMAN SURVIVAL OF MOTOR NEURON 1 (SMN1) GENE
GSRS Full Record:

  • 2609078-43-3
  • DNA (recombinant adeno-associated virus vector pAAV-SMN1-GeneBeam v2020-03-11 cytomegalovirus enhancer region plus cytomegalovirus promoter region plus human β-globin gene intron fragment plus human survival of motor neuron protein SMN1 codon-optimized gene plus human somatotropin gene polyadenylation signal plus adeno-associated virus 2 inverted terminal repeat flanks)
  • Pasemnogene gleparvovec transgene insert encoding codon-optimised human survival of motor neuron 1 (SMN1) gene



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