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BOTARETIGENE SPAROPARVOVEC

UNII:IIO8Q82SD1
Type:INGREDIENT SUBSTANCE
Formula:
Preferred Substance Name:BOTARETIGENE SPAROPARVOVEC
GSRS Full Record:

  • 2417551-39-2
  • AAV-RPGR
  • BOTARETIGENE SPAROPARVOVEC [USAN]
  • Botaretigene sparoparvovec [WHO-DD]
  • DNA (RECOMBINANT PSEUDOTYPED ADENO-ASSOCIATED VIRUS 5 VECTOR AAV-RPGR HUMAN RHODOPSIN KINASE PROMOTER FRAGMENT-REGULATED HUMAN RETINITIS PIGMENTOSA GTPASE REGULATOR RPGR-ORF15 ISOFORM GENE VARIANT PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS)
  • botaretigene sparoparvovec [INN]



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