FDA official logo
GSRS logoPFDA official logo

DALNACOGENE PONPARVOVEC TRANSGENE INSERT

UNII:HX2RYV9JXP
Type:INGREDIENT SUBSTANCE
Formula:
Preferred Substance Name:DALNACOGENE PONPARVOVEC TRANSGENE INSERT
GSRS Full Record:

  • Dalnacogene ponparvovec transgene insert
  • Dalnacogene ponparvovec transgene insert encoding a codon-optimised (CpG reduced) gain of function variant (Padua variant; R338L) of human coagulation factor IX




UNII - HX2RYV9JXP | UNII Search Service