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ZOCAGLUSAGENE NUZAPARVOVEC

UNII:FDB4GQ8A3Y
Type:INGREDIENT SUBSTANCE
Formula:
Preferred Substance Name:ZOCAGLUSAGENE NUZAPARVOVEC
GSRS Full Record:

  • 2601264-52-0
  • AT-845
  • AT845
  • DNA (recombinant adeno-associated virus vector AT845 mouse muscle-type creatine kinase enhancer plus mouse muscle-type creatine kinase promoter plus human lysosomal α-glucosidase precursor codon-optimized transgene plus simian virus 40 polyadenylation signal plus adeno-associated virus 2 inverted terminal repeat flanks-specifying)
  • Recombinant, non-replicating adeno-associated virus serotype 8 (rAAV8) vector encoding codon-optimized human acid alpha-glucosidase (GAA), also called lysosomal α-glucosidase or acid maltase, under control of a mouse muscle creatine kinase (MCK) enhancer/promoter followed by a simian virus 40 (SV40) intron, terminated by the SV40 late polyadenylation sequence, and flanked by AAV2 inverted terminal repeats (ITRs)
  • ZOCAGLUSAGENE NUZAPARVOVEC [USAN]
  • Zocaglusagene Nuzaparvovec
  • zocaglusagene nuzaparvovec [INN]



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