CROSIGALCOGENE OMLIXPARVOVEC

UNII:	AFM8985FXH
Type:	INGREDIENT SUBSTANCE
Formula:
Preferred Substance Name:	CROSIGALCOGENE OMLIXPARVOVEC
GSRS Full Record:	AFM8985FXH i

2607030-09-9
Crosigalcogene Omlixparvovec
Crosigalcogene omlixparvovec (recombinant, non-replicating adeno-associated virus serotype hu68 (AAVhu68) vector encoding codon-optimised human galactosylceramidase (GALC), under control of a cytomegalovirus immediate early enhancer/chicken β-actin promoter (the CB7 promoter) plus a chimeric intron, consisting of a chicken β-actin splice donor and a rabbit β-globin splice acceptor, terminated with a rabbit β-globin polyadenylation signal, flanked by adeno-associated virus 2 (AAV2) inverted terminal repeats (ITRs))
DNA (recombinant replication-defective adeno-associated virus serotype hu68 vector PBKR03 cytomegalovirus enhancer fusion with chicken β-actin promoter plus chicken β-actin intron plus human galactosylceramidase codon-optimized gene GALC plus rabbit β-globin polyadenylation signal plus adeno-associated virus 2 inverted terminal repeat flanks)
crosigalcogene omlixparvovec [INN]

Note

UNIIs are generated based on scientific identity characteristics using ISO 11238 data elements. UNII availability does not imply any regulatory review or approval. Synonyms and mappings are based on the best public information available at the time of publication. Please report any problems/errors associated with this data to FDA-SRS@fda.hhs.gov.

CROSIGALCOGENE OMLIXPARVOVEC

Synonyms and Mappings

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