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INLEZIFIGENE CIVAPARVOVEC

UNII:87RN2MR2FP
Type:INGREDIENT SUBSTANCE
Formula:
Preferred Substance Name:INLEZIFIGENE CIVAPARVOVEC
GSRS Full Record:

  • 2143578-31-6
  • A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS TYPE 2/6 (RAAV REP2-CAP6) VECTOR, EXPRESSING A CDNA THAT TARGETS 447-461 BP OF THE ALBUMIN LOCUS (RELATIVE TO THE TRANSCRIPTION INITIATION SITE), FUSED TO THE OBLIGATE HETERODIMERIC FOKI NUCLEASE DOMAIN ELD, UNDER THE CONTROL OF AN APOLIPOPROTEIN E HEPATIC CONTROL REGION AND HUMAN ALPHA-1-ANTITRYPSIN PROMOTER (APOE/HAAT)
  • inlezifigene civaparvovec [INN]



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