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ROSTUDIRSEN

UNII:3AR55D4G2D
Type:INGREDIENT SUBSTANCE
Formula:
Preferred Substance Name:ROSTUDIRSEN
GSRS Full Record:

  • 3028750-59-3
  • (5’-C-T-C-C-A-A-C-A-T-C-A-A-G-G-A-A-G-A-T-G-G-C-A-T-T-T-C-T-A-G), 5’-[P-(4-{4-[(2-Amino-2-oxoethyl)(methyl)amino]-6-[(6-aminohexyl)oxy]-1,3,5-triazin-2-yl}piperazin-1-yl)]-N,N-dimethylphosphonamidate
  • RNA, [P-deoxy-P-(dimethylamino)](2′,3′-dideoxy-2′,3′-imino-2′,3′-seco)(2′a→5′)(Cm5U-C-C-A-A-C-A-m5U-C-A-A-G-G-A-A-G-A-m5U-G-G-C-A-m5U-m5U-m5U-C-m5U-AG), 5′-[P-[4-[4-[(2-amino-2-oxoethyl)methylamino]-6-[[6-[[[[4-[[N-[3-[2-[2-[2-[(5aS,6R,6aR)-6-(18-carboxy-3-oxo-2,7,10,13,16-pentaoxa-4-azaoctadec-1-yl)-5,5a,6,6a,7,8-hexahydrocyclopropa[5,6]cycloocta[1,2-d]-1,2,3-triazol-1(4H)-yl]ethoxy]ethoxy]ethoxy]-1-oxopropyl]-L-valyl-N5(aminocarbonyl)-Lornithyl]amino]phenyl]methoxy]carbonyl]amino]hexyl]oxy]-1,3,5-triazin-2-yl]-1-piperazinyl]-N,N-dimethylphosphonamidate].
  • ROSTUDIRSEN [USAN]
  • Rostudirsen
  • Zeleciment rostudirsen oligonucleotid-lysine modification



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