FDA official logo
GSRS logoPFDA official logo

RIVUNATPAGENE MIZIPARVOVEC

UNII:24Q8LJQ6Y2
Type:INGREDIENT SUBSTANCE
Formula:
Preferred Substance Name:RIVUNATPAGENE MIZIPARVOVEC
GSRS Full Record:

  • 2646715-00-4
  • DNA (recombinant replication-defective adeno-associated virus serotype 9 vector UX701 murine transthyretin enhancer plus human transthyretin promoter plus simian virus 40 intron plus human adenosine triphosphatase copper-transporting β metal-binding domain 4/5/6 transgene ATP7B-MBD456 plus simian virus 40 polyadenylation signal plus adeno-associated virus 2 inverted terminal repeat flanks plus adeno-associated virus 2 Rep region plus adeno-associated virus 9 Cap region-specifying)
  • RIVUNATPAGENE MIZIPARVOVEC [USAN]
  • Rivunatpagene Miziparvovec
  • UX-701
  • UX701
  • recombinant, non-replicating adeno-associated virus serotype 9 (rAAV9) vector encoding ATPase copper-transporting beta gene (ATP7B, copper transporting ATPase 2), modified to encode the last three of the six metal-binding domains (ATP7B-MBD456), under control of a murine transthyretin enhancer/human transthyretin promoter, with a simian virus 40 (SV40) intron, terminated with an SV40 polyadenylation signal, and flanked by adeno-associated virus 2 (AAV2) inverted terminal repeats (ITRs)
  • rivunatpagene miziparvovec [INN]



UNII - 24Q8LJQ6Y2 | UNII Search Service